Duchenne Muscular Dystrophy

US & EU Yearly Sales Potential

According to Capricor DMD affects 20,000 boys and young men in the US.

CAPR management states the cost will be around $150,000/dose with 4 doses required (every 3 mo.) per year.

Source

Total Addressable US Market

20,000 patients x 50% market penetration x $600,000/treatment* = $6B/year (peak sales)

*

Total Addressable EU Market

The EU market is often very similar to the US market but larger in this instance.

24,000 patients x 50% market penetration x $400,000/treatment* = $4.8B/year (peak sales)

Total Rest of World (ROW) Market (just an estimage by FN)

100,000 patients x 10% market penetration x $300,000/treatment* = $3B/year (peak sales)

* ROW pricing would be less than US & EU

In summary the total DMD global market could be well over $10B! (peak sales)